| 20080213182 | Methods and Compositions for Treatment of Diseases Associated with Aberrant Microsatellite Expansion - The present invention provides methods and compositions for the treatment of diseases associated with aberrant microsatellite expansions. Methods of the present invention comprise the use of recombinant adeno-associated virus vectors containing a transgene encoding at least one muscleblind protein. The present invention also provides an animal model for a disease associated with aberrant microsatellite expansion. | 09-04-2008 |
