GMP-ORPHAN
GMP-ORPHAN Patent applications | ||
Patent application number | Title | Published |
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20140187638 | PHENYLBUTYRATE IN RECTAL FORM FOR THE TREATMENT OF A MOTOR NEURON DISEASE OR A METABOLIC DISEASE - The present invention relates to rectal administration of phenylbutyrate for treating a motor neuron disease, such as, for example, spinal muscular atrophy or a metabolic disease such as, for example, an urea cycle disorder, related methods and compositions. | 07-03-2014 |